PPIDT00451

Drug Information
NameAgalsidase alfa
SequenceLDNGLARTPTMGWLHWERFMCNLDCQEEPDSCISEKLFMEMAELMVSEGWKDAGYEYLCIDDCWMAPQRDSEGRLQADPQRFPHGIRQLANYVHSKGLKLGIYADVGNKTCAGFPGSFGYYDIDAQTFADWGVDLLKFDGCYCDSLENLADGYKHMSLALNRTGRSIVYSCEWPLYMWPFQKPNYTEIRQYCNHWRNFADIDDSWKSIKSILDWTSFNQERIVDVAGPGGWNDPDMLVIGNFGLSWNQQVTQMALWAIMAAPLFMSNDLRHISPQAKALLQDKDVIAINQDPLGKQGYQLRQGDNFEVWERPLSGLAWAVAMINRQEIGGPRSYTIAVASLGKGVACNPACFITQLLPVKRKLGFYEWTSRLRSHINPTGTVLLQLENTMQMSLKDLL
DrugBank_IDDB15874
Typebiotech
IndicationAgalsidase alfa is indicated in the treatment of Fabry disease.[L16398]

Dosage Forms
Form Route Strength
Capsule Oral
600 umol/1
Injection, solution, concentrate Intravenous
1 MG/ML
Solution Intravenous
1 mg / mL
Solution, concentrate Intravenous
3.5 mg
Solution Intravenous
1.0 mg/mL
Target Information
Role Uniprot_ID Gene_Name Entity_Name Organism Actions Internal link
transporter P20645 M6PR Cation-dependent mannose-6-phosphate receptor Homo sapiens substrate Link